BioMarin will discontinue dosing and enrollment of its phase 2 trials for Voxzogo—currently approved in achondroplasia, a ...

Annualized height velocity of 9.05 cm/year (LS mean) for TransCon hGH-treated children was similar at Week 52 to daily somatropin-treated ...

BioMarin will stop dosing in Phase II trials of the drug in Turner Syndrome, SHOX-deficiency and Aggrecan deficiency.

With Ascendis Pharma entering the achondroplasia space last month and BridgeBio on deck, BioMarin faces competition. Adding to the pressure, the company suffered a setback Monday when it halted two ...

I am treating a 4-year-old with Turner syndrome and type 1 diabetes. She has no malformations, her height is 92 cm, and her metabolic control is excellent (HbA1c, 6%). Her parents have been informed ...

March 16 (Reuters) - BioMarin Pharmaceutical will discontinue mid-stage trials of its bone disorder treatment after reports of several cases of patients' hip joint slipping out of place, the drugmaker ...

Liliana Castaneda, with Turner syndrome, was diagnosed with rare clear cell carcinoma of the vagina at 14, unrelated to her condition. Her treatment involved five chemotherapy rounds, external beam ...

I receive many emails from twins and their families with important stories to tell. In October 2025, I received a message from a fraternal female twin to say that she had a twin sister with Turner ...

APEX, N.C. (WTVD) -- Despite being a pharmacist, Dan Patriss first learned of Turner syndrome after his daughter was diagnosed at 4 years old. It's a genetic condition caused by a missing or altered X ...

Dublin, March 13, 2026 (GLOBE NEWSWIRE)-- The "Accretropin Market Report 2026: Epidemiology, Pipeline Analysis, Market Insights & Forecasts" has been added to ResearchAndMarkets.com's offering. The ...